Cre-dependent selection yields AAV variants for widespread gene transfer to the adult brain BE Deverman, PL Pravdo, BP Simpson, SR Kumar, KY Chan, A Banerjee, ... Nature biotechnology 34 (2), 204-209, 2016 | 996 | 2016 |
Targeted long-read sequencing captures CRISPR editing and AAV integration outcomes in brain BP Simpson, CM Yrigollen, A Izda, BL Davidson Molecular Therapy 31 (3), 760-773, 2023 | 17 | 2023 |
CRISPR–Cas Gene Editing for Neurological Disease BP Simpson, BL Davidson Nervous System Drug Delivery, 365-376, 2019 | 2 | 2019 |
Compositions and methods for treating fragile X syndrome and related syndromes BL Davidson, CM Yrigollen, A Monteys, B Simpson US Patent 11,497,816, 2022 | | 2022 |
Crispr/cas9 gene editing of atxn2 for the treatment of spinocerebellar ataxia type 2 B Simpson, B Davidson, AM Monteys US Patent App. 17/594,651, 2022 | | 2022 |
The Molecular and Behavioral Phenotypes Altered in CGG Knock-In Mice Edited Using CRISPR CM Yrigollen, B Simpson, E Lim, YH Chen, B Davidson MOLECULAR THERAPY 30 (4), 135-135, 2022 | | 2022 |
Long-Read Nanopore Sequencing Reveals Outcomes of AAV-CRISPR Editing in the Brain of Transgenic Mouse Models BP Simpson, CM Yrigollen, PT Ranum, BL Davidson MOLECULAR THERAPY 30 (4), 390-391, 2022 | | 2022 |
Using Nanopore Sequencing to Characterize On-Target CRISPR-Mediated Gene Editing BP Simpson, CM Yrigollen, PT Ranum, BL Davidson MOLECULAR THERAPY 28 (4), 278-279, 2020 | | 2020 |
CRISPR-Cas9 Gene Editing Strategies of ATXN2 for the Treatment of Spinocerebellar Ataxia Type 2 BP Simpson, MS Keiser, AM Monteys, BL Davidson MOLECULAR THERAPY 27 (4), 112-112, 2019 | | 2019 |
252. Using Cre-Dependent In Vivo Selection to Identify AAV Variants That Enable Efficient and Widespread Gene Transfer to the Adult Central Nervous System BE Deverman, PL Pravdo, BP Simpson, SR Kumar, Y Luo, KY Chan, ... Molecular Therapy 24, S99, 2016 | | 2016 |
Engineering Recombinant AAV Vectors for More Efficient and Restricted Gene Expression in the CNS after Systemic Administration BE Deverman, B Simpson, P Pravdo, A Banerjee, PH Patterson MOLECULAR THERAPY 22, S118-S118, 2014 | | 2014 |