| Precise therapeutic gene correction by a simple nuclease-induced double-stranded break S Iyer, S Suresh, D Guo, K Daman, JCJ Chen, P Liu, M Zieger, K Luk, ... Nature 568 (7753), 561-565, 2019 | 115 | 2019 |
| Aerobic glycolysis is essential for normal rod function and controls secondary cone death in retinitis pigmentosa L Petit, S Ma, J Cipi, SY Cheng, M Zieger, N Hay, C Punzo Cell reports 23 (9), 2629-2642, 2018 | 109 | 2018 |
| Editing out five Serpina1 paralogs to create a mouse model of genetic emphysema F Borel, H Sun, M Zieger, A Cox, B Cardozo, W Li, G Oliveira, A Davis, ... Proceedings of the National Academy of Sciences 115 (11), 2788-2793, 2018 | 83 | 2018 |
| Genetic Deficiency of Flavin-Containing Monooxygenase 3 (Fmo3) Protects Against Thrombosis but Has Only a Minor Effect on Plasma Lipid Levels—Brief Report DM Shih, W Zhu, RC Schugar, Y Meng, X Jia, A Miikeda, Z Wang, ... Arteriosclerosis, thrombosis, and vascular biology 39 (6), 1045-1054, 2019 | 51 | 2019 |
| Understanding the cephalic eyes of pulmonate gastropods: a review MV Zieger, VB Meyer-Rochow American Malacological Bulletin 26 (1/2), 47-66, 2008 | 46 | 2008 |
| Systemic Delivery of AAVB1-GAA Clears Glycogen and Prolongs Survival in a Mouse Model of Pompe Disease AM Keeler, M Zieger, SH Todeasa, AL McCall, JC Gifford, S Birsak, ... Human Gene Therapy 30 (1), 57-68, 2019 | 37 | 2019 |
| CX3CL1 (Fractalkine) Protein Expression in Normal and Degenerating Mouse Retina: In Vivo Studies M Zieger, PK Ahnelt, P Uhrin PloS one 9 (9), e106562, 2014 | 35 | 2014 |
| Muscle-directed delivery of an AAV1 vector leads to capsid-specific T cell exhaustion in nonhuman primates and humans G Gernoux, AM Gruntman, M Blackwood, M Zieger, TR Flotte, C Mueller Molecular Therapy 28 (3), 747-757, 2020 | 32 | 2020 |
| Improved cell metabolism prolongs photoreceptor survival upon retinal-pigmented epithelium loss in the sodium iodate induced model of geographic atrophy M Zieger, C Punzo Oncotarget 7 (9), 9620, 2016 | 32 | 2016 |
| Intralingual and intrapleural AAV gene therapy prolongs survival in a SOD1 ALS mouse model AM Keeler, M Zieger, C Semple, L Pucci, A Veinbachs, RH Brown, ... Molecular Therapy-Methods & Clinical Development 17, 246-257, 2020 | 26 | 2020 |
| Airway smooth muscle dysfunction in Pompe (Gaa−/−) mice AM Keeler, D Liu, M Zieger, L Xiong, J Salemi, K Bellvé, BJ Byrne, ... American Journal of Physiology-Lung Cellular and Molecular Physiology 312 (6 …, 2017 | 23 | 2017 |
| Eyes and vision in Arion rufus and Deroceras agreste (Mollusca; Gastropoda; Pulmonata): What role does photoreception play in the orientation of these terrestrial … MV Zieger, IA Vakoliuk, OP Tuchina, VV Zhukov, VB Meyer‐Rochow Acta Zoologica 90 (2), 189-204, 2009 | 23 | 2009 |
| The eye of the freshwater prosobranch gastropod Viviparus viviparus: ultrastructure, electrophysiology and behaviour VV Zhukov, SL Borissenko, MV Zieger, IA Vakoliuk, VB Meyer‐Rochow Acta Zoologica 87 (1), 13-24, 2006 | 21 | 2006 |
| Evaluation of cytosine base editing and adenine base editing as a potential treatment for alpha-1 antitrypsin deficiency MS Packer, V Chowdhary, G Lung, LI Cheng, Y Aratyn-Schaus, ... Molecular Therapy 30 (4), 1396-1406, 2022 | 20 | 2022 |
| AAV9 gene replacement therapy for respiratory insufficiency in very‐long chain acyl‐CoA dehydrogenase deficiency M Zieger, AM Keeler, TR Flotte, MK ElMallah Journal of inherited metabolic disease 42 (5), 870-877, 2019 | 8 | 2019 |
| Liver-directed SERPINA1 gene therapy attenuates progression of spontaneous and tobacco smoke-induced emphysema in α1-antitrypsin null mice M Zieger, F Borel, C Greer, G Gernoux, M Blackwood, TR Flotte, C Mueller Molecular Therapy-Methods & Clinical Development 25, 425-438, 2022 | 7 | 2022 |
| Generation of alpha-1 antitrypsin knockout and PI* ZZ ferrets using Crispr/Cas9. A genetic model of emphysema N He, BH Rosen, JS Gray, IA Evans, M Zieger, Z Yan, F Borel, B Liang, ... Annals of the American Thoracic Society 15 (Supplement 4), S292-S293, 2018 | 3 | 2018 |
| Liver-Directed Gene Therapy for Lung Disease in Alpha1 Antitrypsin Deficiency M Zieger, C Greer, TR Flotte, C Mueller MOLECULAR THERAPY 28 (4), 572-572, 2020 | 1 | 2020 |
| Use of Adenine Base Editors to Precisely Correct the Disease-Causing PiZ Mutation in Alpha-1 Antitrypsine Deficiency M Packer, V Chowdhary, G Lung, LI Cheng, Y Aratyn-Schaus, S Smith, ... MOLECULAR THERAPY 28 (4), 311-312, 2020 | 1 | 2020 |
| Citrullination, a novel post-translational modification of elastin, is involved in COPD Pathogenesis MP Murphy, M Zieger, M Henry, P Meleady, C Mueller, NG McElvaney, ... American Journal of Physiology-Lung Cellular and Molecular Physiology, 2024 | | 2024 |
