| Base editing rescue of spinal muscular atrophy in cells and in mice M Arbab, Z Matuszek, KM Kray, A Du, GA Newby, AJ Blatnik, A Raguram, ... Science 380 (6642), eadg6518, 2023 | 78 | 2023 |
| A novel function for Foxm1 in interkinetic nuclear migration in the developing telencephalon and anxiety-related behavior X Wu, X Gu, X Han, A Du, Y Jiang, X Zhang, Y Wang, G Cao, C Zhao Journal of Neuroscience 34 (4), 1510-1522, 2014 | 25 | 2014 |
| Foxg1 Directly Represses Dbx1 to Confine the POA and Subsequently Regulate Ventral Telencephalic Patterning A Du, X Wu, H Chen, QR Bai, X Han, B Liu, X Zhang, Z Ding, Q Shen, ... Cerebral Cortex 29 (12), 4968-4981, 2019 | 16 | 2019 |
| Improved gene therapy for spinal muscular atrophy in mice using codon-optimized hSMN1 transgene and hSMN1 gene-derived promotor Q Xie, X Chen, H Ma, Y Zhu, Y Ma, L Jalinous, GF Cox, F Weaver, J Yang, ... EMBO Molecular Medicine 16 (4), 945-965, 2024 | 9 | 2024 |
| Non-canonical amino acid incorporation into AAV5 capsid enhances lung transduction in mice H Chang, A Du, J Jiang, L Ren, N Liu, X Zhou, J Liang, G Gao, D Wang Molecular Therapy Methods & Clinical Development 31, 2023 | 8 | 2023 |
| Producing high-quantity and high-quality recombinant adeno-associated virus by low-cis triple transfection H Liu, Y Zhang, M Yip, L Ren, J Liang, X Chen, N Liu, A Du, J Wang, ... Molecular Therapy Methods & Clinical Development 32 (2), 2024 | 5 | 2024 |
| Base editing rescue of spinal muscular atrophy in cells and in mice. Science 380, eadg6518 M Arbab, Z Matuszek, KM Kray, A Du, GA Newby, AJ Blatnik, A Raguram, ... | 5 | 2023 |
| Systemic gene therapy corrects the neurological phenotype in a mouse model of NGLY1 deficiency A Du, K Yang, X Zhou, L Ren, N Liu, C Zhou, J Liang, N Yan, G Gao, ... JCI insight 9 (19), e183189, 2024 | | 2024 |
| Gene replacement therapy for foxg1 syndrome D Wang, G Gao, A Du US Patent App. 17/910,574, 2023 | | 2023 |
