Targeted exon skipping with AAV-mediated split adenine base editors J Winter, A Luu, M Gapinske, S Manandhar, S Shirguppe, WS Woods, ... Cell discovery 5 (1), 41, 2019 | 48 | 2019 |
Targeting Duchenne muscular dystrophy by skipping DMD exon 45 with base editors M Gapinske, J Winter, D Swami, L Gapinske, WS Woods, S Shirguppe, ... Molecular Therapy-Nucleic Acids 33, 572-586, 2023 | 3 | 2023 |
Protein engineering technologies for development of next-generation genome editors J Winter, S Shirguppe, P Perez-Pinera Current Opinion in Biomedical Engineering, 100514, 2023 | 1 | 2023 |
In vivo CRISPR base editing for treatment of Huntington′ s disease S Shirguppe, M Gapinske, D Swami, N Gosstola, P Acharya, A Miskalis, ... bioRxiv, 2024.07. 05.602282, 2024 | | 2024 |
SPLICER: A Highly Efficient Base Editing Toolbox That Enables In Vivo Therapeutic Exon Skipping A Miskalis, S Shirguppe, J Winter, G Elias, D Swami, A Nambiar, M Stilger, ... bioRxiv, 2024.04. 01.587650, 2024 | | 2024 |
Development of Platforms to Target HTT In Vivo Using Base Editing Technologies S Shirguppe, M Gapinske, D Swami, P Acharya, D Anand, D Joulani, ... MOLECULAR THERAPY 30 (4), 298-298, 2022 | | 2022 |