Choice of template delivery mitigates the genotoxic risk and adverse impact of editing in human hematopoietic stem cells S Ferrari, A Jacob, D Cesana, M Laugel, S Beretta, A Varesi, G Unali, ... Cell Stem Cell 29 (10), 1428-1444. e9, 2022 | 66 | 2022 |
HDAC8 regulates canonical Wnt pathway to promote differentiation in skeletal muscles L Ferrari, C Bragato, L Brioschi, M Spreafico, S Esposito, A Pezzotta, ... Journal of Cellular Physiology 234 (5), 6067-6076, 2019 | 12 | 2019 |
Intrathymic AAV delivery results in therapeutic site-specific integration at TCR loci in mice A Calabria, C Cipriani, G Spinozzi, L Rudilosso, S Esposito, F Benedicenti, ... Blood, The Journal of the American Society of Hematology 141 (19), 2316-2329, 2023 | 6 | 2023 |
Late phases of hematopoietic reconstitution in metachromatic leukodystrophy gene therapy patients are characterized by lineage commitment of individual HSC clones A Calabria, G Spinozzi, F Benedicenti, D Cesana, L Del Core, E Tenderini, ... MOLECULAR THERAPY 28 (4), 234-234, 2020 | 2 | 2020 |
Adaptive Routes of Hematopoietic Stem Cell Differentiation to Disease Conditions and Age in Gene Therapy Patients A Calabria, G Spinozzi, D Cesana, F Benedicenti, G Pais, S Scala, ... Blood 140 (Supplement 1), 1904-1905, 2022 | 1 | 2022 |
Next-generation ex-vivo gene editing of human hematopoietic stem cells by optimized delivery platforms and selection of cells bearing the intended edits S Ferrari, A Jacob, M Fiumara, V Vavassori, D Cesana, D Canarutto, ... HUMAN GENE THERAPY 33 (23-24), A149-A149, 2022 | | 2022 |
Hematopoietic Reconstitution and Lineage Commitment in HSC-GT Patients are Influenced by the Disease Background A Calabria, G Spinozzi, F Benedicenti, D Cesana, G Pais, S Scala, ... MOLECULAR THERAPY 30 (4), 173-174, 2022 | | 2022 |
Sonication Linker Mediated-PCR (SLiM-PCR), an Efficient Method for Quantitative Retrieval of Vector Integration Sites F Benedicenti, A Calabria, D Cesana, A Albertini, S Esposito, G Pais, ... MOLECULAR THERAPY 30 (4), 412-412, 2022 | | 2022 |
High Frequency of AAV Integration at Double Strand Breaks Induced in Preclinical Model of Gene Therapy and in Edited Long-Term Engrafted HSPCs A Calabria, C Cipriani, G Spinozzi, S Esposito, F Benedicenti, A Albertini, ... MOLECULAR THERAPY 30 (4), 7-7, 2022 | | 2022 |
Hematopoietic reconstitution and lineage commitment in HSC GT patients are influenced by the disease background A Calabria, G Spinozzi, F Benedicenti, D Cesana, S Scala, S Scaramuzza, ... HUMAN GENE THERAPY 32 (19-20), A84-A85, 2021 | | 2021 |
Hematopoietic Reconstitution and Lineage Commitment in HSC Gene Therapy Patients Are Influenced by the Disease Background A Calabria, G Spinozzi, F Benedicenti, D Cesana, L Del Core, S Scala, ... MOLECULAR THERAPY 29 (4), 42-42, 2021 | | 2021 |