| Precise correction of the dystrophin gene in duchenne muscular dystrophy patient induced pluripotent stem cells by TALEN and CRISPR-Cas9 HL Li, N Fujimoto, N Sasakawa, S Shirai, T Ohkame, T Sakuma, ... Stem cell reports 4 (1), 143-154, 2015 | 655 | 2015 |
| Concordant but varied phenotypes among Duchenne muscular dystrophy patient-specific myoblasts derived using a human iPSC-based model IY Choi, HT Lim, K Estrellas, J Mula, TV Cohen, Y Zhang, CJ Donnelly, ... Cell reports 15 (10), 2301-2312, 2016 | 168 | 2016 |
| Efficient genomic correction methods in human iPS cells using CRISPR–Cas9 system HL Li, P Gee, K Ishida, A Hotta Methods 101, 27-35, 2016 | 84 | 2016 |
| Genetic correction using engineered nucleases for gene therapy applications H Lisa Li, T Nakano, A Hotta Development, growth & differentiation 56 (1), 63-77, 2014 | 59 | 2014 |
| Epithelial Sodium Channel ENaC is a Modifier of the Long Term Non-progressive Phenotype Associated with F508del CFTR Mutations. GC Agrawal PB, Wang R, Li HL, Schmitz-Abe K, Simone-Roach C, Chen J, Shi J ... American Journal of Respiratory Cell and Molecular Biology, 2017 | 39 | 2017 |
| Pluripotent stem cell model of Nakajo-Nishimura syndrome untangles proinflammatory pathways mediated by oxidative stress F Honda-Ozaki, M Terashima, A Niwa, N Saiki, Y Kawasaki, H Ito, A Hotta, ... Stem cell reports 10 (6), 1835-1850, 2018 | 32 | 2018 |
| Concordant but varied phenotypes among Duchenne muscular dystrophy patient-specific myoblasts derived using a human iPSC-based model. Cell Rep 15 (10): 2301–2312 IY Choi, H Lim, K Estrellas, J Mula, TV Cohen, Y Zhang, CJ Donnelly, ... doi. org/10.1016/j. celre p 16, 2016 | 8 | 2016 |
| Editing Cultured Human Cells: From Cell Lines to iPS Cells HL Li, A Hotta Targeted Genome Editing Using Site-Specific Nucleases: ZFNs, TALENs, and the …, 2015 | 3 | 2015 |
| Concordant but varied phenotypes among Duchenne muscular dystrophy patient-specific myoblasts derived using a human iPSC-based model. Cell Rep. 2016; 15 (10): 2301–12 IY Choi, HT Lim, K Estrellas, J Mula, TV Cohen, Y Zhang | 3 | |
| Engineered nuclease mediated genetic correction in iPSCs derived from Duchenne muscular dystrophy patient HL Li, N Fujimoto, N Sasakawa, S Shirai, T Yamamoto, K Woltjen, ... MOLECULAR THERAPY 22, S124-S124, 2014 | 2 | 2014 |
| 571. Precise Control of CRISPR-Cas9 Mediated Gene Editing for Correcting Mutation of Duchenne Muscular Dystrophy in iPS Cells HL Li, N Sasakawa, K Ishida, P Gee, A Hotta Molecular Therapy 23, S227, 2015 | | 2015 |
