| RAN proteins and RNA foci from antisense transcripts in C9ORF72 ALS and frontotemporal dementia T Zu, Y Liu, M Bañez-Coronel, T Reid, O Pletnikova, J Lewis, TM Miller, ... Proceedings of the National Academy of Sciences 110 (51), E4968-E4977, 2013 | 865 | 2013 |
| C9orf72 BAC mouse model with motor deficits and neurodegenerative features of ALS/FTD Y Liu, A Pattamatta, T Zu, T Reid, O Bardhi, DR Borchelt, AT Yachnis, ... Neuron 90 (3), 521-534, 2016 | 390 | 2016 |
| Modulation of histone deacetylase 6 (HDAC6) nuclear import and tubulin deacetylase activity through acetylation Y Liu, L Peng, E Seto, S Huang, Y Qiu Journal of Biological Chemistry 287 (34), 29168-29174, 2012 | 152 | 2012 |
| RAN translation regulated by muscleblind proteins in myotonic dystrophy type 2 T Zu, JD Cleary, Y Liu, M Bañez-Coronel, JL Bubenik, F Ayhan, ... Neuron 95 (6), 1292-1305. e5, 2017 | 137 | 2017 |
| Variant-selective stereopure oligonucleotides protect against pathologies associated with C9orf72-repeat expansion in preclinical models Y Liu, JC Dodart, H Tran, S Berkovitch, M Braun, M Byrne, AF Durbin, ... Nature communications 12 (1), 847, 2021 | 58 | 2021 |
| Vorinostat: a potent agent to prevent and treat laser-induced corneal haze A Tandon, JCK Tovey, MR Waggoner, A Sharma, JW Cowden, DJ Gibson, ... Journal of Refractive Surgery 28 (4), 285-290, 2012 | 41 | 2012 |
| Impact of guanidine-containing backbone linkages on stereopure antisense oligonucleotides in the CNS P Kandasamy, Y Liu, V Aduda, S Akare, R Alam, A Andreucci, D Boulay, ... Nucleic acids research 50 (10), 5401-5423, 2022 | 33 | 2022 |
| Preclinical evaluation of WVE-004, an investigational stereopure oligonucleotide for the treatment of C9orf72-associated ALS or FTD Y Liu, A Andreucci, N Iwamoto, Y Yin, H Yang, F Liu, A Bulychev, XS Hu, ... Molecular Therapy-Nucleic Acids 28, 558-570, 2022 | 31 | 2022 |
| Development of a sensitive trial-ready poly (GP) CSF biomarker assay for C9orf72-associated frontotemporal dementia and amyotrophic lateral sclerosis KM Wilson, E Katona, I Glaria, M Carcolé, IJ Swift, A Sogorb-Esteve, ... Journal of Neurology, Neurosurgery & Psychiatry 93 (7), 761-771, 2022 | 16 | 2022 |
| Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT N Iwamoto, Y Liu, M Frank-Kamenetsky, A Maguire, WC Tseng, K Taborn, ... Molecular Therapy-Nucleic Acids, 2024 | | 2024 |
