Safety of Intravenous Administration of an AAV8 Vector Coding for an Oxidation-Resistant Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency

JB Rosenberg, BP De, A Greco, N Gorman… - Human Gene …, 2023 - liebertpub.com
α1-antitrypsin (AAT) deficiency is a common autosomal recessive hereditary disorder, with a
high risk for the development of early-onset panacinar emphysema. AAT, produced primarily …

Safety of Intravenous Administration of an AAV8 Vector Coding for an Oxidation-Resistant Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency.

JB Rosenberg, BP De, A Greco, N Gorman… - Human Gene …, 2023 - europepmc.org
Abstract α1-antitrypsin (AAT) deficiency is a common autosomal recessive hereditary
disorder, with a high risk for the development of early-onset panacinar emphysema. AAT …

Safety of Intravenous Administration of an AAV8 Vector Coding for an Oxidation-Resistant Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency

JB Rosenberg, P De Bishnu, A Greco… - Human gene …, 2023 - pubmed.ncbi.nlm.nih.gov
α1-antitrypsin (AAT) deficiency is a common autosomal recessive hereditary disorder, with a
high risk for the development of early-onset panacinar emphysema. AAT, produced primarily …

[HTML][HTML] Safety of Intravenous Administration of an AAV8 Vector Coding for an Oxidation-Resistant Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency

JB Rosenberg, BP De, A Greco, N Gorman… - Human Gene …, 2023 - ncbi.nlm.nih.gov
Abstract α1-antitrypsin (AAT) deficiency is a common autosomal recessive hereditary
disorder, with a high risk for the development of early-onset panacinar emphysema. AAT …

Safety of Intravenous Administration of an AAV8 Vector Coding for an Oxidation Resistant Human α1-antitrypsin for the Treatment of α1-antitrypsin Deficiency.

JB Rosenberg, BP De, A Greco, N Gorman… - Human Gene …, 2023 - europepmc.org
α1-antitrypsin (AAT) deficiency is a common autosomal recessive hereditary disorder, with a
high risk for the development of early onset panacinar emphysema. AAT produced primarily …