Intracerebral Administration of Adeno-Associated Viral Vector Serotype rh.10 Carrying Human SGSH and SUMF1 cDNAs in Children with Mucopolysaccharidosis …

M Tardieu, M Zérah, B Husson… - Human gene …, 2014 - liebertpub.com
Mucopolysaccharidosis type IIIA is a severe degenerative disease caused by an autosomal
recessive defect of a gene encoding a lysosomal heparan-N-sulfamidase, the N …

Intracerebral administration of adeno-associated viral vector serotype rh. 10 carrying human SGSH and SUMF1 cDNAs in children with mucopolysaccharidosis type …

M Tardieu, M Zérah, B Husson… - Human Gene …, 2014 - europepmc.org
Mucopolysaccharidosis type IIIA is a severe degenerative disease caused by an autosomal
recessive defect of a gene encoding a lysosomal heparan-N-sulfamidase, the N …

[PDF][PDF] Intracerebral Administration of Adeno-Associated Viral Vector Serotype rh. 10 Carrying Human SGSH and SUMF1 cDNAs in Children with …

M Tardieu, M Zérah, B Husson… - HUMAN GENE …, 2014 - academia.edu
Mucopolysaccharidosis type IIIA is a severe degenerative disease caused by an autosomal
recessive defect of a gene encoding a lysosomal heparan-N-sulfamidase, the N …

[引用][C] Intracerebral Administration of Adeno-Associated Viral Vector Serotype rh.10 Carrying Human SGSH and SUMF1 cDNAs in Children with …

M Tardieu, M Zérah, B Husson, S de Bournonville… - Human Gene …, 2014 - cir.nii.ac.jp
Intracerebral Administration of Adeno-Associated Viral Vector Serotype rh.10 Carrying Human
<i>SGSH</i> and <i>SUMF1</i> cDNAs in Children with Mucopolysaccharidosis Type IIIA …

Intracerebral Administration of Adeno-Associated Viral Vector Serotype rh. 10 Carrying Human SGSH and SUMF1 cDNAs in Children with Mucopolysaccharidosis …

M Tardieu, B Husson, S de Bournonville… - HUMAN GENE …, 2014 - iris.unina.it
Mucopolysaccharidosis type IIIA is a severe degenerative disease caused by an autosomal
recessive defect of a gene encoding a lysosomal heparan-N-sulfamidase, the N …

Intracerebral administration of adeno-associated viral vector serotype rh. 10 carrying human SGSH and SUMF1 cDNAs in children with mucopolysaccharidosis type …

M Tardieu, M Zérah, B Husson… - Human gene …, 2014 - pubmed.ncbi.nlm.nih.gov
Mucopolysaccharidosis type IIIA is a severe degenerative disease caused by an autosomal
recessive defect of a gene encoding a lysosomal heparan-N-sulfamidase, the N …

Intracerebral administration of adeno-associated viral vector serotype rh. 10 carrying human SGSH and SUMF1 cDNAs in children with mucopolysaccharidosis type …

M Tardieu, M Zérah, B Husson… - Human Gene …, 2014 - hero.epa.gov
Mucopolysaccharidosis type IIIA is a severe degenerative disease caused by an autosomal
recessive defect of a gene encoding a lysosomal heparan-N-sulfamidase, the N …