W Ngo, J Peukes, A Baldwin, ZW Xue, S Hwang… - Proceedings of the …, 2025 - pnas.org
The widespread application of genome editing to treat and cure disease requires the delivery of genome editors into the nucleus of target cells. Enveloped delivery vehicles …
The urea cycle facilitates the disposal of nitrogen waste and the elimination of harmful ammonia. Argininosuccinic aciduria (ASA), a urea cycle defect caused by a deficiency in …