A transcriptomic-based drug repositioning approach for the identification of novel muscle-specific therapies for spinal muscular atrophy
JM Hoolachan - 2022 - keele-repository.worktribe.com
Spinal muscular atrophy (SMA) is an autosomal recessive neuromuscular disorder (NMD)
caused by depleted survival of motor neuron (SMN) levels and characterised by neuronal …
caused by depleted survival of motor neuron (SMN) levels and characterised by neuronal …