A Alavi, L Krishnamurti, M Abedi, I Galeon, D Reiner… - Blood, 2021 - Elsevier
Introduction Sickle cell disease (SCD) is caused by pathologic variants in both alleles of the
β-globin gene, affecting~ 100,000 patients in the US (Strouse. Handb Clin Neurol 2016; 138 …