A new kid on the playground of CRISPR DMD therapy
D Duan - Human Gene Therapy Clinical Development, 2017 - liebertpub.com
DUCHENNE MUSCULAR DYSTROPHY (DMD) is the most common lethal muscle disease,
affecting approximately 250,000 boys worldwide. The disease is caused by mutations in the …
affecting approximately 250,000 boys worldwide. The disease is caused by mutations in the …