RNA therapeutics (RNATx) aim to treat diseases, including cancer, by targeting or
employing RNA molecules for therapeutic purposes. Amongst the most promising targets …

The successful application of messenger RNA vaccines in the market has demonstrated the
potential of gene therapy in treating various diseases, including infectious diseases …

Neurodegenerative diseases (NDs) demonstrate a complex interaction with the immune
system, challenging the traditional view of the brain as an “immune-privileged” organ …

Nucleic acid therapeutics offer tremendous promise for addressing a wide range of common
public health conditions. However, the in vivo nucleic acids delivery faces significant …

Dysferlin is a large transmembrane protein involved in critical cellular processes including
membrane repair and vesicle fusion. Mutations in the dysferlin gene (DYSF) can result in …

Parkinson's disease (PD) is a neurodegenerative disorder that predominantly affects
dopaminergic neurons in the substantia nigra and ventral tegmental area, resulting in …