Duchenne muscular dystrophy is an X-linked disease caused by the absence of functional
dystrophin in the muscle cells. Major advances have led to the development of gene …

Duchenne muscular dystrophy (DMD) is an X-linked recessive neuromuscular disorder with
a prevalence of approximately 1 in 3500–5000 males. DMD manifests as childhood-onset …

Duchenne muscular dystrophy (DMD) is the most common childhood muscular dystrophy
affecting~ 1: 5000 live male births. Following the identification of pathogenic variations in the …

Duchenne muscular dystrophy (DMD) is a devastating disorder caused by loss of functional
dystrophin protein, resulting in muscle wasting. Enhancing muscle growth by inhibiting …

Duchenne muscular dystrophy (DMD) is a severe X-linked disease characterized by
progressive muscle weakness. It is caused by a variety of DMD gene pathogenic variations …

Duchenne muscular dystrophy (DMD), a rare genetic disorder characterized by progressive
muscle weakness, is caused by the absence or a decreased amount of the muscle …

Duchenne muscular dystrophy (DMD) is typically caused by mutations that disrupt the DMD
reading frame, but nonsense mutations in the 5′ part of the gene induce utilization of an …

Abstract Duchenne Muscular Dystrophy (DMD) is a progressive and fatal muscle-wasting
disease with no known cure. We previously reported the preliminary safety and efficacy up to …

Abstract Duchenne Muscular Dystrophy (DMD) is a lethal disease caused by mutations in
dystrophin encoding gene, causing progressive degeneration of cardiac, respiratory, and …

Abstract Duchenne Muscular Dystrophy (DMD) is a X-linked progressive lethal muscle
wasting disease for which there is no cure. We present first-in-human study assessing safety …