Existing recombinant adeno-associated virus (rAAV) serotypes for delivering in vivo gene
therapy treatments for human liver diseases have not yielded combined high-level human …

“Evaluating the Past and Present of Regenerative Medicine (RM)” was the first part of an
Industry Symposium dedicated to the subject during the 2015 TERMIS World Congress in …

Gene therapy is the only novel technology that currently offers the prospect of a lasting cure
for hemophilia and freedom from the burden of repeated injections. Recent data from a …

Skeletal muscle is ideal for passive vaccine administration as it is easily accessible by
intramuscular injection. Recombinant adeno-associated virus (rAAV) vectors are in …

基因编辑是一种基于人工核酸酶的遗传操作技术, 能精确地对DNA 或RNA 进行高效改造.
基因编辑除了在基础研究, 生物育种和药物筛选等方面展现了巨大前景之外 …

WO2017143100A1 - Novel recombinant adeno-associated virus capsids resistant to pre-existing
human neutralizing antibodies - Google Patents WO2017143100A1 - Novel recombinant …

2018-02-23 Assigned to THE BOARD OF TRUSTEES OF THE LELAND STANFORD
JUNIOR UNIVERSITY reassignment THE BOARD OF TRUSTEES OF THE LELAND …

DISCLOSURES: Navarro is a clinical professor in the College of Pharmacy at the University
of Florida, Gainesville, and is an assistant editor with the Journal of Managed Care and …

THERAPEUTIC GENOME EDITING FOR THE TREATMENT OF GENETIC DISEASES: TESTING
THE SAFETY AND EFFECTIVENESS OF CRISPR/CAS9 THERAPEUTI Page 1 THERAPEUTIC …

Genome editing has facilitated versatile gene modifications in somatic and stem cells.
Despite the early stage, therapeutic uses of ZFN and TALEN have already demonstrated …