The efficacy of naïve versus modified mesenchymal stem cells in improving muscle function in duchenne muscular dystrophy: A systematic review

OYJ Shen, YF Chen, HT Xu, CW Lee - Biomedicines, 2021 - mdpi.com
As one of the most common genetic conditions, Duchenne muscular dystrophy (DMD) is a
fatal disease caused by a recessive mutation resulting in muscle weakness in both voluntary …

Improving clinical trial design for Duchenne muscular dystrophy

L Merlini, P Sabatelli - BMC neurology, 2015 - Springer
Background Currently, the most promising therapies for Duchenne muscular dystrophy
(DMD) are exon skipping and stop codon read-through, two strategies aimed at restoring the …

Current management of Duchenne muscular dystrophy in the Middle East: expert report

MA Jumah, MA Muhaizea, AA Rumayyan… - Neurodegenerative …, 2019 - Taylor & Francis
Aim: Duchenne muscular dystrophy (DMD) is a severe and rare X-linked neuromuscular
childhood disorder that results in functional decline, loss of ambulation and early death due …

Neuromuscular Scoliosis: An Overview

B Yaszay, KM Coe, BP Scannell - … of Spinal Disorders in Young Children, 2022 - Springer
Progressive neurologic and muscular diseases can cause progressive and severe scoliosis.
Some of these diseases include Duchenne muscular dystrophy, arthrogryposis multiplex …

[PDF][PDF] Early diagnosis and treatment–the use of Ataluren in the effective management of Duchenne muscular dystrophy

E Mercuri, R Quinlivan, S Tuffery-Giraud - Eur Neurol Rev, 2018 - academia.edu
The understanding of the natural history of Duchenne muscular dystrophy (DMD) is
increasing rapidly and new treatments are emerging that have the potential to substantially …

[PDF][PDF] A Study of Development of Pseudohypertrophisms in a Patient with Duchenne Muscular Dystrophy

R Dehankar, U Bhakare, DD Ksheersagar… - Int. J. Curr. Res …, 2016 - researchgate.net
Hypertrophy is the abnormal enlargement of a body part or organ, especially when
bodybuilder or athletes take androgenic hormone, likes steroids, androgen, corticoids the …