Genetic approaches for the treatment of facioscapulohumeral muscular dystrophy
KRQ Lim, T Yokota - Frontiers in Pharmacology, 2021 - frontiersin.org
Facioscapulohumeral muscular dystrophy (FSHD) is an autosomal dominant disorder
characterized by progressive, asymmetric muscle weakness at the face, shoulders, and …
characterized by progressive, asymmetric muscle weakness at the face, shoulders, and …
[HTML][HTML] Oligonucleotide Therapies for Facioscapulohumeral Muscular Dystrophy: Current Preclinical Landscape
Facioscapulohumeral muscular dystrophy (FSHD) is an inherited myopathy, characterized
by progressive and asymmetric muscle atrophy, primarily affecting muscles of the face …
by progressive and asymmetric muscle atrophy, primarily affecting muscles of the face …
Transplantation of PSC-derived myogenic progenitors counteracts disease phenotypes in FSHD mice
Facioscapulohumeral muscular dystrophy (FSHD) is a genetically dominant progressive
myopathy caused by improper silencing of the DUX4 gene, leading to fibrosis, muscle …
myopathy caused by improper silencing of the DUX4 gene, leading to fibrosis, muscle …
Electroporation: An Effective Method For In Vivo Gene Delivery
A Nikyar, A Bolhassani - Drug Delivery Letters, 2022 - ingentaconnect.com
Background: Gene therapy is a promising approach for the treatment of various diseases,
including cancer, hereditary disorders, and some viral infections. The development of …
including cancer, hereditary disorders, and some viral infections. The development of …
Current strategies of muscular dystrophy therapeutics: an overview
KRQ Lim, T Yokota - Muscular Dystrophy Therapeutics: Methods and …, 2022 - Springer
Muscular dystrophies are a group of genetic disorders characterized by varying degrees of
progressive muscle weakness and degeneration. They are clinically and genetically …
progressive muscle weakness and degeneration. They are clinically and genetically …
The DUX4–HIF1α Axis in Murine and Human Muscle Cells: A Link More Complex Than Expected
TH Nguyen, M Limpens, S Bouhmidi… - International Journal of …, 2024 - mdpi.com
FacioScapuloHumeral muscular Dystrophy (FSHD) is one of the most prevalent inherited
muscle disorders and is linked to the inappropriate expression of the DUX4 transcription …
muscle disorders and is linked to the inappropriate expression of the DUX4 transcription …
Development of Antisense Therapies for Facioscapulohumeral and Duchenne Muscular Dystrophy
KRQ Lim - 2021 - era.library.ualberta.ca
Facioscapulohumeral muscular dystrophy (FSHD) and Duchenne muscular dystrophy
(DMD) are two of the most commonly inherited muscular disorders in the world. There is …
(DMD) are two of the most commonly inherited muscular disorders in the world. There is …